Interactive Genomic Exploration · Neurodegeneration

The Genetics of Alzheimer's

An interactive journey through the human genome to understand why amyloid and tau build up in the brain — and what role the APOE gene plays.

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Risk loci (GWAS)
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Heritability (twin studies)
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Genes curated in this atlas
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Key cellular mechanisms
The story at a glance

From genes to memory loss

The whole journey of this page, summed up in steps.

Starting point
Genes + age (APP · PSEN · APOE)
First hallmark
Amyloid-β builds up (plaques)
Second hallmark
Tau forms tangles
Immune response
Inflammation (microglia)
Damage
Neuronal death
Where
Hippocampus and cortex
Outcome
Memory loss
The disease

What is Alzheimer's disease?

Before getting into the genetics, it helps to understand the disease these genes help explain.

Alzheimer's disease is the most common cause of dementia: a neurodegenerative disease in which the brain accumulates amyloid-β plaques and tau tangles, becomes inflamed and loses neurons, above all in the hippocampus and the cortex. The most typical early symptom is episodic memory loss. The vast majority are late-onset cases driven by genes (especially APOE), age and lifestyle.

#1 dementia
It is the most common cause of dementia worldwide
~1 in 9
People over 65 are living with Alzheimer's
APOE ε4
Greatest common genetic risk factor for late-onset Alzheimer's
~75 loci
Genome regions associated with risk (GWAS, 2022)
Origin

From the first described case to the disease

In 1906, the physician Alois Alzheimer presented the case of Auguste Deter, a woman with early-onset dementia in whose brain he observed under the microscope the plaques and tangles that define the disease today. Decades later, amyloid, tau and the genes that modulate risk were identified — the starting point for the rest of this page.

Symptoms

More than "forgetfulness"

The disease progresses in stages and affects several domains, which vary from one person to another:

First

Episodic memory

Forgetting recent facts and conversations, repeating questions and becoming disoriented in time. It reflects the early damage to the hippocampus.

Later

Executive function and language

Difficulty planning, solving problems, finding words and orienting in space, as it spreads to the cortex.

Throughout

Behavioral and psychiatric

Apathy, anxiety, depression, irritability and, in advanced stages, agitation, sleep disturbances or delusions.

Profiles

It is not a single disease

Common (>95%)

Sporadic late-onset

Appears from age 65 onward. It does not follow simple inheritance: it depends on many common risk genes (especially APOE), age and lifestyle.

Rare (<5%)

Early-onset familial

Before age 65, sometimes in the forties. Caused by autosomal dominant mutations in APP, PSEN1 or PSEN2: each child has a 50% risk of inheriting them.

Special case

Alzheimer's in Down syndrome

With three copies of chromosome 21 there is an extra dose of the APP gene: amyloid pathology is almost universal and Alzheimer's appears at early ages.

Over the course of the disease

A slow, progressive process

Brain changes begin years before the first symptoms. Clinical progression is usually described in stages:

Preclinical

Brain changes are already present (amyloid, tau), but the person has no symptoms. Detectable only through biomarkers.

Mild cognitive impairment

Noticeable memory lapses that do not yet interfere with daily life. Not everyone progresses to dementia.

Mild dementia

Forgetfulness that affects everyday life, difficulties with words and orientation. This is usually when diagnosis happens.

Moderate dementia

Greater dependence: confusion, behavioral changes and the need for help with everyday tasks.

Severe dementia

Loss of communication and autonomy; total dependence and continuous care.

Treatment

No cure, but options that are changing

There is no treatment that cures the disease, but there are drugs and supports that improve symptoms and, for the first time, therapies that act on its biology:

Symptoms

Symptomatic drugs

Cholinesterase inhibitors (donepezil, rivastigmine, galantamine) and memantine: improve or stabilize symptoms for a time, without slowing the cause.

Recent disease-modifiers

Anti-amyloid antibodies

Lecanemab and donanemab clear amyloid and modestly slow decline in early stages. They require monitoring for adverse effects (ARIA).

People and families

Support and caregivers

Cognitive stimulation, adapting the environment, managing vascular factors and, above all, support for caregivers: cornerstones of management.

Educational content with a scientific basis (Alzheimer 1906; the amyloid hypothesis; the GWAS of Bellenguez et al. 2022; lecanemab, van Dyck et al. 2023). It does not replace assessment by a healthcare professional.

Foundation

What is DNA?

DNA (deoxyribonucleic acid) is the molecule that stores the genetic instructions of every living thing, spread across about 3 billion base pairs.

Four bases — A, T, C and G — form the double helix. In Alzheimer's, certain variants alter how the brain produces and clears amyloid and how its immune system responds, raising the risk of neurodegeneration.

A — Adenine
T — Thymine
C — Cytosine
G — Guanine
Interactive

Explore the genome

Alzheimer's genes are scattered across the whole genome. Click a chromosome to see its regions, the evidence and the genes involved.

Gene atlas

Gene catalog

Causal and risk genes of Alzheimer's disease. Search and filter by cellular mechanism; click a card to see its function and the studies.

Functional convergence

Cellular mechanisms

Alzheimer's genes converge on just a few brain processes. Hover over a node to identify the gene; click to see the detail.

More than a century of science

Timeline of discoveries

From the first case described by Alois Alzheimer to the 75 risk loci and the anti-amyloid antibodies.

Biology

Biological processes involved

How Alzheimer's genes drive amyloid plaques, tau tangles and the brain's immune response.

What the data say

Is Alzheimer's inherited?

Alzheimer's is highly heritable — twin studies estimate around 70% — but only a small fraction follows simple familial inheritance.

0%
Heritability (twin studies)
0%
Autosomal dominant familial forms (early-onset)

Fewer than 5% are early-onset forms caused by mutations in APP, PSEN1 or PSEN2. In late-onset Alzheimer's (the vast majority), the most powerful common genetic factor is the APOE ε4 allele, which can multiply the risk several times over.

Risk associated with APOE ε4 (homozygotes, approx.)up to ~12×

Even with two copies of ε4 many people never develop the disease: age, vascular factors and lifestyle also matter.

Conclusions

What do we know for certain?

The essentials about the genetics of Alzheimer's disease:

The key point: inheriting the APOE ε4 allele raises the risk, but it is not a sentence. Genetics guides prevention and, today, guides the first anti-amyloid therapies.

Where it strikes

The hippocampus and the cortex

Alzheimer's does not damage the brain evenly: it begins in the memory regions and spreads to the rest of the cortex. Click a region to see its role.

hippocampus
Where it begins Atrophies later Relatively preserved
Interactive · APOE risk

Your APOE genotype and relative risk

The APOE gene has three variants (ε2, ε3, ε4) and you inherit one from each parent. Choose a combination to see how the relative risk changes compared with ε3/ε3 (the most common reference).

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Approximate relative risk (vs. ε3/ε3)

Indicative figures (based on Corder et al. 1993 and later meta-analyses; they vary with population, sex and age). APOE ε4 is a risk factor, not destiny: many people with ε4 never develop Alzheimer's, and many without ε4 do.

Therapeutic avenues: where does each one stand?
Already in clinical use

Symptoms and, now, amyloid

  • Symptomatic: cholinesterase inhibitors and memantine
  • Approved anti-amyloid: lecanemab and donanemab (early stages)
  • Management of vascular factors and caregiver support
In clinical trials

Beyond amyloid

  • Anti-tau therapies (antibodies, antisense)
  • Anti-inflammatory approaches targeting microglia (TREM2)
  • Prevention in carriers of mutations or of APOE ε4
Preclinical research

The next targets

  • Gene editing and APOE modulation
  • New targets in microglia, lipids and endocytosis
  • Drug combinations and blood-based biomarkers
Myths

What does NOT cause Alzheimer's

It helps to separate science from myths and distinguish modifiable risk from false causes:

Aluminum (cookware, deodorants) "Forgetting things = Alzheimer's" It is a normal part of aging Vaccines Using your brain "too little"

An isolated lapse is not Alzheimer's, and aging does not mean you will develop it. There is a real modifiable risk: managing blood pressure, diabetes and hearing, exercising, not smoking and staying physically, mentally and socially active reduces the risk, though it does not eliminate it.

The frontier

The latest and what's coming

After a century of hypotheses, genetics and biomarkers are transforming how Alzheimer's is detected and treated.

Recent advances

Discoveries that are changing the field

Treating the cause

Anti-amyloid antibodies

In 2023, lecanemab showed for the first time a clear clinical benefit by clearing amyloid, confirming its causal role. Donanemab followed soon after: the era of disease-modifiers has begun, though with modest effects.

Detecting earlier

Blood-based biomarkers

Blood tests such as p-tau217 can detect Alzheimer's pathology without a lumbar puncture or PET, opening the door to an early and accessible diagnosis.

Tailored treatment

Precision medicine

Polygenic risk scores together with the APOE genotype are beginning to guide whom and when to treat or enroll in prevention trials.

Future directions

Where research is heading

Second hallmark

Anti-tau therapies

Because tau correlates better with symptoms, halting its aggregation and spread is one of the major goals of the next generation of drugs.

Immunity

Modulating microglia

Acting on TREM2 and other immune targets to help the brain clear amyloid and tau without harming neurons.

Early window

Preventing before symptoms

With biomarkers and genetics, treating in the preclinical phase — before decline appears — could be the most effective strategy.

Research is moving fast and some of these results are recent: dates and specific figures may change as the trials mature.

Frequently asked questions

Common questions

The questions that come up most when learning about the genetics of Alzheimer's.

Is Alzheimer's hereditary?
Partly. It is highly heritable (twin studies estimate ~70%), but fewer than 5% follow simple familial inheritance (APP, PSEN1, PSEN2). In the vast majority — late-onset Alzheimer's — what is inherited is a predisposition spread across many common risk genes, above all APOE.
I have APOE ε4 — does that mean I'll get Alzheimer's?
No. APOE ε4 is the greatest common genetic risk factor, but it is risk, not certainty: many people with ε4 (even two copies) never develop the disease, and many without ε4 do. Age, vascular factors and lifestyle also matter.
Can it be prevented?
There is no guaranteed way to avoid it, but there are ways to reduce the risk: managing blood pressure, diabetes, cholesterol and hearing, exercising, not smoking, sleeping well and staying mentally and socially active. An important part of the risk is modifiable.
Are Alzheimer's and dementia the same thing?
No. Dementia is a general term for the loss of cognitive functions that interferes with daily life; it has many causes. Alzheimer's is the most common cause of dementia, but there are others (vascular, Lewy body, frontotemporal...).
Is there a test to know if I have it or will get it?
There are tests that support the diagnosis (amyloid and tau biomarkers in cerebrospinal fluid or PET, and new blood tests such as p-tau217). The APOE genetic test gives a risk, not a diagnosis, and is only recommended with genetic counseling.
Do the new drugs cure Alzheimer's?
They do not cure it. Anti-amyloid antibodies (lecanemab, donanemab) modestly slow decline in early stages by clearing amyloid, but they do not reverse the damage and require monitoring for adverse effects. They are a first step, not a cure.
Sources and glossary

Where this comes from

Milestones and scientific sources this page is based on.

Foundational milestones
1906Alzheimer A. Über eine eigenartige Erkrankung der Hirnrinde. The first case (Auguste Deter): plaques and tangles.
1991Goate A et al. Segregation of a missense mutation in the amyloid precursor protein gene with familial Alzheimer's disease. Nature. First mutation (APP) and the amyloid hypothesis.
1993Corder EH, Strittmatter WJ et al. Gene dose of apolipoprotein E type 4 allele and the risk of Alzheimer's disease. Science. APOE ε4 as a risk factor.
1995Sherrington R et al. Cloning of a gene bearing missense mutations in early-onset familial Alzheimer's disease (PSEN1). Nature. The presenilins.
Modern genetics and therapy
2022Bellenguez C et al. New insights into the genetic etiology of Alzheimer's disease and related dementias. Nature Genetics. The map of ~75 risk loci (GWAS).
2023van Dyck CH et al. Lecanemab in early Alzheimer's disease. N Engl J Med. Clinical benefit of the anti-amyloid antibody.
Databases and support
DBsOMIM #104300, AlzGene/IGAP and associations such as the Alzheimer's Association.

An educational synthesis page; it is not a primary clinical source. For medical decisions, consult professionals and the official resources on Alzheimer's.

Glossary

Key terms

Amyloid-βPeptide that accumulates to form the plaques, the first hallmark of the disease.
It is generated when the APP protein is cut by the secretases. When it is overproduced or poorly cleared, it aggregates into plaques outside the neurons. It is the target of the new antibodies (lecanemab, donanemab).
TauA protein that, when altered, forms the tangles inside neurons.
Normally it stabilizes the microtubules. In Alzheimer's it becomes hyperphosphorylated and accumulates in neurofibrillary tangles. Tau burden correlates better with symptoms than amyloid does.
APOELipid-transport gene; its ε4 variant is the greatest common risk.
It has three forms: ε2 (protective), ε3 (neutral, the most common) and ε4 (risk). It influences how the brain clears amyloid. Inheriting ε4 raises the risk, but does not guarantee the disease.
PlaquesDeposits of amyloid-β between the neurons.
They are one of the two pathological hallmarks. They accumulate outside the neurons and were the first thing Alois Alzheimer observed under the microscope in 1906.
TanglesKnots of tau inside the neurons.
The second pathological hallmark. They form inside the neurons from hyperphosphorylated tau and spread through the brain following a characteristic pattern.
MicrogliaThe brain's immune system; many risk genes act in it.
They are the brain's resident immune cells. They try to clear amyloid, but their dysfunction contributes to the disease. Genes such as TREM2 or CD33 place microglia at the center of Alzheimer's.
Sporadic vs. familialThe common (late-onset) form versus the rare (early-onset, inherited) one.
The sporadic late-onset form (>95%) depends on many genes and on age. The familial early-onset form (<5%) is caused by dominant mutations in APP, PSEN1 or PSEN2, with a 50% risk per child.
HippocampusA key memory structure; where the damage usually begins.
It is essential for forming new memories. That is why Alzheimer's begins with episodic memory loss: the hippocampus is among the first regions to atrophy.
BiomarkerA measurable signal of the disease (in blood, fluid or imaging).
It allows Alzheimer's pathology to be detected even before symptoms. Examples: amyloid and tau in cerebrospinal fluid, PET, and new blood tests such as p-tau217.
Test what you've learned

Interactive quiz

Six questions to check what you take away. It grades itself: tap an answer and you'll instantly see whether you're right, with the explanation.

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